Doctors successfully treated a baby with the first ever personalized gene-editing therapy

The team of doctors and scientists, for the first time, was successfully treated with a unique genetic situation with individual genetic therapy. The results of groundbreaking treatment were in New England Medical Magazineaccompanied Earlier, the FDA was further forgotten by a doctor forgotten efforts to regulate gene therapy.

The patient with this date During the first week, a baby was born with CPS1 deficiency, which was about 50 percent of death. Patients who live living can get acquainted with severe brain disease, mental and developmental delays and potential liver transplantation. His care group has prepared a technology for changing the DNA, prepared individual genulization treatment based on a crisp technology.

Successful gene repair for KJ, the discovery of crisp and human genome sequence, which allows the previous federally-funded medical research, including mutation.

This approach to Gene editing can be used potentially to help patients in the future patients with other genetic disorders such as cell disease, cystic fibrosis, Huntington disease and muscle dystrophy. Has already received a couple of crispy drugs For the treatment of sickle cell diseases, but there is a lot of potential investigated in this area.